Huntington's disease treated for first time
Source
Hacker News
Published
TL;DR
AI GeneratedDoctors have successfully treated Huntington's disease for the first time, slowing its progression by 75% in patients. The treatment involves gene therapy delivered through delicate brain surgery, aiming to reduce levels of the toxic huntingtin protein that kills neurons. Results from the trial involving 29 patients showed a significant slowing of the disease and preservation of brain cells. The therapy is considered safe, with plans to seek licensing in the US in 2026. While the treatment is a breakthrough, its high cost and complexity may limit widespread availability.