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Huntington's disease treated for first time

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Hacker News

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Doctors have successfully treated Huntington's disease for the first time, slowing its progression by 75% in patients. The treatment involves gene therapy delivered through delicate brain surgery, aiming to reduce levels of the toxic huntingtin protein that kills neurons. Results from the trial involving 29 patients showed a significant slowing of the disease and preservation of brain cells. The therapy is considered safe, with plans to seek licensing in the US in 2026. While the treatment is a breakthrough, its high cost and complexity may limit widespread availability.

Huntington's disease treated for first time - Tech News Aggregator